Genetics

Nijmegen breakage syndrome

Blepharophimosis ptosis and epicanthus inversus syndrome

Genes H

LAMA3 gene

POR gene

Stargardt macular degeneration

ALG1 gene

HSPG2 gene

PLAGL1 gene

KRT12 gene

DICER1 gene

What are CAR T cell therapy RNA therapy and other genetic therapies